Child Examinations | North Tonawanda, NY

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Cleveland Clinic Children's Among First Hospitals to Use Novel Gene Therapy to Treat Inherited Blood Disorders

Cleveland Clinic Children's is among the first in the country to administer a new gene therapy to modify a patient's blood-forming stem cells in patients with thalassemia. The one-time treatment can reduce or eliminate the need for ongoing blood transfusions.

May 20, 2025


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